CRISPR injected into the blood treats a genetic disease for first time | Science

A brand-new CRISPR-based treatment for a unusual, lethal liver disease depends upon an injection including both a messenger RNA encoding a DNA-cutting enzyme (white) and another RNA (blue) that... Read more »

Decades after a tragic failure, gene therapy successfully treats a rare liver disease | Science

Josh McQuillin, displayed in 2019, 1 year after being dealt with, states gene therapy has actually changed his life. © VIT SIMANEK/CTK PHOTO/ALAMY LIVE NEWS Twenty-2 years earlier, among... Read more »